Bioactive Small Molecules

C5

C5 (click to show)

C5 (click to hide)

Title:

A GAA repeat expansion reporter model of Friedreich\'s ataxia recapitulates the genomic context and allows rapid screening of therapeutic compounds.

Reference:

Hum Mol Genet. 2013 Dec 20;22(25):5173-87. doi: 10.1093/hmg/ddt370. Epub 2013 Aug 13.

Authors:

Lufino MM, Silva AM, Németh AH, Alegre-Abarrategui J, Russell AJ, Wade-Martins R.

Compounds:

C5 (5358626)